Hope in Motion for H-ABC Kids

When Frankie, a child with the rare, devastating brain condition H-ABC, never walked and lost developmental milestones, his mom Amy Sheridan-Hill refused to accept the grim prognosis. Fueled by grief and determination, she teamed up with geneticist Dr. Michelle Teng to launch the H-ABC Foundation and co-found SynaptixBio, a biotech company racing to develop a gene therapy using antisense oligonucleotides. Preclinical results are promising, but the road to human trials is long and expensive—requiring millions and years of work. With time running out for kids like Frankie, this team is fighting to turn science into hope before it’s too late. Support the show:Get a discount at https://solipillow.com/discount/dnn. Advertise on DNN:[email protected] This is an automated, high-level news summary based on public reporting.Report issues to [email protected]. View sources & latest updates:https://sources.thednn.ai/af4b4f81e2adc1a8