Alexander Disease Research Update - Episode #4 - case report, clinical trials

Send us Fan MailAlbee Messing and Amy Waldman discuss the following recent publication: [00:40]             Amano E, Yoshida T, Mizuta I, Oyama J, Sakashita S, Ueyama S, Machida A, Yokota T. (2021). Activation of a Cryptic Splice Site of GFAP in a Patient With Adult-Onset Alexander Disease. Neurology Genetics. 7, e626 PMCID: PMC8488758Florian Eichler joins for a discussion about outcomes and clinical trials, prompted by:[13:09]             Questions from emailSend your questions and feedback to:  [email protected] support research on Alexander Disease at the University of Wisconsin-Madison's Waisman Center:           https://alexander-disease.waisman.wisc.edu/donate/