Current and Emerging ERTs/SRTs
from Rare Discussions Hosted by CheckRare Editors
This CME/CE activity, hosted by Ozlem Goker-Alpan, MD, Co-founder and President Lysosomal & Rare Disorders Research & Treatment Center (LDRTC) and Neal J Weinreb, MD, FACP, Voluntary Associate Professor of Human Genetics, University of Miami Miller School of Medicine, highlights how enzyme replacement therapies (ERTs) and substrate reduction therapies (SRTs) for lysosomal storage disorders have transformed, and will continue to transform, the treatment landscape for these rare conditions. At the end of this activity, participants should be able to: • Describe how ERTs/SRTs have transformed the LSD population • Describe the new research underway to improve safety and efficacy of ERTs/SRTs • Describe how ERTs/SRTs are addressing the problem of the blood brain barrier Educational Support for this activity was provided by Takeda, Sanofi, and Cheisi. To obtain CME credit, please visit https://checkrare.com/learning-center/courses/ Rare Discussions is produced by CheckRare, the leading multimedia platform dedicated to advancing education, awareness, and innovation across the rare disease community. Explore additional physician interviews, podcasts, CME activities, and rare disease resources at CheckRare.com. Subscribe to the CheckRare Podcast Network for expert conversations, weekly news, accredited education, and the latest advances across the rare disease community. Part of the CheckRare Podcast Network: Trusted conversations, news, education, and expert insights across the rare disease community.
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