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Ep. 179 - DMD Gene Therapies, CBER & NIH episode artwork

EPISODE · May 23, 2023 · 27 MIN

Ep. 179 - DMD Gene Therapies, CBER & NIH

from BioCentury This Week · host BioCentury

If FDA approves Sarepta's gene therapy for Duchenne muscular dystrophy, patients will soon face the difficult choice between taking this treatment or waiting for a better option among the “unprecedented” amount of innovation ahead in DMD, as taking both may not be an option, BioCentury Executive Director Lauren Martz said on the latest BioCentury This Week podcast. Martz and colleagues assess the landscape for DMD gene therapies ahead of the May 29 PDUFA date for delandistrogene moxeparvovec.Also on the show, BioCentury Washington Editor Steve Usdin discusses takeaways from his conversation with FDA's Peter Marks; three tasks for Monica Bertagnolli to prioritize at NIH; and what the debt ceiling means for the life sciences. And on the heels of Bio€quity Europe, Editor in Chief Simone Fishburn delivers her insights from BioCentury’s European conference.This week’s podcast is sponsored by Cancer Research Horizons.Reach us by sending a text

What this episode covers

If FDA approves Sarepta's gene therapy for Duchenne muscular dystrophy, patients will soon face the difficult choice between taking this treatment or waiting for a better option among the “unprecedented” amount of innovation ahead in DMD, as taking both may not be an option, BioCentury Executive Director Lauren Martz said on the latest BioCentury This Week podcast. Martz and colleagues assess the landscape for DMD gene therapies ahead of the May 29 PDUFA date for delandistrogene moxeparvovec....

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Ep. 179 - DMD Gene Therapies, CBER & NIH

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Frequently Asked Questions

How long is this episode of BioCentury This Week?

This episode is 27 minutes long.

When was this BioCentury This Week episode published?

This episode was published on May 23, 2023.

What is this episode about?

If FDA approves Sarepta's gene therapy for Duchenne muscular dystrophy, patients will soon face the difficult choice between taking this treatment or waiting for a better option among the “unprecedented” amount of innovation ahead in DMD, as taking...

Can I download this BioCentury This Week episode?

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