Future Therapies in Galactosaemia - JIMD Podcasts

What this episode covers

The podcast welcomes Professor Maria Estela Rubio-Gozalbo and welcomes back Professor Judy Fridovich-Keil to talk mRNA therapy, gene therapy and disease models in classic galactosemia. Novel mRNA therapy restores GALT protein and enzyme activity in a zebrafish model of classic galactosemia Britt Delnoy, et al https://doi.org/10.1002/jimd.12512 Neonatal GALT gene replacement offers metabolic and phenotypic correction through early adulthood in a rat model of classic galactosemia Jennifer M. I. Daenzer, et al https://doi.org/10.1002/jimd.12471

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Frequently Asked Questions

How long is this episode of JIMD Podcasts?

This episode is 39 minutes long.

When was this JIMD Podcasts episode published?

This episode was published on August 12, 2022.

What is this episode about?

The podcast welcomes Professor Maria Estela Rubio-Gozalbo and welcomes back Professor Judy Fridovich-Keil to talk mRNA therapy, gene therapy and disease models in classic galactosemia. Novel mRNA therapy restores GALT protein and enzyme activity...

Can I download this JIMD Podcasts episode?

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