Lost in translation — Challenges in drug development for rare disease

Robin Lachmann and Marc Patterson return to the podcast and are joined by their collaborator Dr Sandra Sirrs, to talk about their recent Editorial on drug development in rare disease. Lost in translation—Challenges in drug development for inherited metabolic diseases Robin H. Lachmann, Marc C. Patterson, and Sandra Sirrs https://doi.org/10.1002/jimd.12501