EPISODE · Mar 2, 2022 · 8 MIN
Onasemnogene abeparvovec, gene therapy, and the hierarchy of evidence
from Pharmacy Microteaches · host Dave Abbott
Gene therapy - it's here, and it's really expensive! What does onasemnogene abeparvovec do? How does how it works compare to other (also complicated and expensive) medicines? How strong can the evidence be if it's not from a randomised controlled trial? And, probably most importantly, why on earth does it have 10 syllables in its name and how might you go about butchering its pronunciation?
What this episode covers
Gene therapy - it's here, and it's really expensive! What does onasemnogene abeparvovec do? How does how it works compare to other (also complicated and expensive) medicines? How strong can the evidence be if it's not from a randomised controlled trial? And, probably most importantly, why on earth does it have 10 syllables in its name and how might you go about butchering its pronunciation?
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Onasemnogene abeparvovec, gene therapy, and the hierarchy of evidence
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