Tofersen dans la SLA-SOD1 episode artwork

EPISODE · Jan 6, 2026 · 4 MIN

Tofersen dans la SLA-SOD1

from La biblio Neuro · host Dr Nicolas Landragin

Cette étude présente les résultats finaux de l'essai clinique VALOR et de son extension, évaluant le tofersen comme traitement pour les adultes atteints de SLA liée au gène SOD1.Miller TM, Cudkowicz ME, Shaw PJ, Genge A, Sobue G, Bucelli RC, et al. Long-Term Tofersen in SOD1 Amyotrophic Lateral Sclerosis. JAMA Neurol. 2025Hébergé par Ausha. Visitez ausha.co/politique-de-confidentialite pour plus d'informations.

Episode metadata supplied by the publisher feed · Published Jan 6, 2026

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