All Episodes

From Innovation to Access: Patient Advocacy as a Strategic Partner with Sara Johnson Davis

Using AI to Drive Innovation in CGT with Le Cong, PhD

The biological clock of aging and the possibility of lifespan extension with Christin Glorioso and John Bell

Against the Odds: How Dr. Anna Maurer Built a Life in Science

A Discussion on the Past, Present, and Future Promise of Gene Editing with Fyodor Urnov, PhD

How rare diseases are shaping therapeutic innovation with Jennifer Adair, Claire Booth, Terry Flotte and Donald Kohn

A Full-Circle Journey at Stanford: Get to Know ASGCT President Matthew Porteus, PhD

Member Minutes: Godwin Iroanya

Setting the Stage: Meet the New Voices Behind The Issue

Member Minutes: Dylan Bechtle

Development of a secretable frataxin for Friedrich’s ataxia with Dr. Dan DuBreuil

Member Minutes: Mark Deehan, PhD

Member Minutes: Chrissy Green

A CFTR mRNA isoform for the treatment of 3’ CFTR PTC variants with Normand Allaire

Member Minutes: Marco Carpenter, PhD

Soundbites Featuring Jennifer Adair, PhD; Motahareh Arjomandnejad, PhD; Rachel Cunningham, PhD; Dr. George Ssenyange, MD; and Gertrude N. Kiwanuka, PhD

Soundbites Featuring Daria Fedyukina, PhD

Soundbites Featuring Hans-Peter Kiem, MD, PhD

Soundbites Featuring Defne Amado, MD, PhD

Soundbites Featuring Craig Martin

Soundbites Featuring Dawn Bowles, PhD

Soundbites Featuring Claire Booth, MBBS, PhD

Soundbites Featuring Jon Whitton, PhD

Soundbites Featuring Sarah Ellinwood, Cynthia Clayton, and Lori Lennon

Soundbites Featuring Dr. Timothy Yu

Soundbites Featuring Dr. Justin Eyquem

Soundbites Featuring Dr. Andrew Wilber

ASGCT 2026 Abstract Highlights with Emily Walsh Martin, Sanjay D’Souza, and Jason West

The Issue – A Caregiver’s Journey from Development to Treatment with Amber Freed, Founder of SLC6A1 Connect

Key Considerations of Gene Therapy Development: A Caregiver's Story

CGMP iPSC-derived myogenic progenitor product for the treatment of muscular dystrophies with Joseph Glorioso and Rita Perlingeiro

The Issue – Prepared under pressure: Navigating the due diligence process with Dr. Ralph Brandenberger

mRNA-based CAR T cell engineering with Norman Drzeniek and Niklas Kotzian

The Issue - Evolving Patient Access to CGTs via Innovation in Medicaid Reimbursement Models with Melissa Majerol

Cas9-CLIPT-mediated integration of large transgenes with Krishanu Saha, Anna Tommasi, and Dan Cappabianca

RNA interference gene therapy for Parkinson’s disease with Kathy Steece-Collier, Jeffrey Kordower, and Fredric Manfredsson

The Issue - Entrepreneurship, Fundraising, and the Future of Cell & Gene Therapy with Dr. Niki Paulk

The Issue - Unlocking New Therapeutic Potential: Ensoma’s Platform for Rare Disease and Oncology

2025 Year in Review with the Molecular Therapy Family of Journals

Generating CAR T cells in vivo with lentiviral vectors with Drs. Rachael Nimmo and Kyriacos Mitrophanous

A Molecular Glue Degrader to Control CRISPR with Drs. Krishanu Saha and Namita Khajanchi

Lipid Nanoparticles with Drs. Daniel Stone, Harrison Dulin, and Keith R. Jerome - The Molecular Therapy Podcast

Patients Are the Center with Kimberly Haugstad, MBA

25 Years of Molecular Therapy with Drs. Rayne Rouce and Joe Glorioso

Building a Vision for Disease Prevention + Treatment with Dr. Mimi Lee

A Vaccine for Cocaine Addiction with Dr. Stephen Kaminsky

25 Years of Molecular Therapy with Drs. Beverly Davidson and Jeff Chamberlain

Developing Therapeutic Platforms with Dr. P.J. Brooks

The Ups and Downs of Conducting Groundbreaking Research with Dr. Kiran Musunuru

25 Years of Molecular Therapy with Sheila Mikhail and Dr. Mark Kay

25 Years of Molecular Therapy with Drs. Terry Flotte and Carl June

The Importance of Long-term Data with Dolan Sondhi, PhD - The Issue

The When, What, How, and Why of FDA Engagement with Niki Gallo - The Issue

Incorporating miRNAs into a taRNA vector platform with Drs. Tim Beissert and Ayşegül Yildiz - The Molecular Therapy Podcast

Trust, Innovation, and the Power of Patient Advocacy with Brendan Hayes - ASGCT's The Issue

Setting Safety Parameters in Gene Therapy Trials with Thomas Wechsler – The Issue

RNA Exon Editing with Ascidian Therapeutics' Drs. Robert Bell and Michael Ehlers - The Molecular Therapy Podcast

Cell Therapy Development for Solid Tumors with AffyImmune's Sonal Gupta, MD, PhD - The Issue

Single-chain Antibody-directed Herpes Simplex Viruses with Joseph Glorioso, PhD - The Molecular Therapy Podcast

cGMP and Building Cohesive Teams with Christopher Choi, PhD, Roswell Park Comprehensive Cancer Center - The Issue

A New Era of Molecular Therapy with Joseph Glorioso, PhD

Non-AAV, Non-rare Gene Therapy with Derek Jackson, Pacira BioSciences–The Issue

The Intersection of Ethics and Gene Therapy with Dr. Ben Hurlbut–The Issue

CRISPR Editing and AAV Integration in the Brain with Drs. Beverly Davidson and Bryan Simpson—The Molecular Therapy Podcast

CRISPR and Beyond with Vertex CSO David Altshuler, MD, PhD—ASGCT's The Issue

Targeting STAT3 in Tumors with Oligo-PROTAC with Dr. Marcin Kortylewski—The Molecular Therapy Podcast

AAV Capsid Production with Drs. Mario Mietzsch and Robert McKenna - Molecular Therapy Podcast

Gene Insertion Tech with Jason Cole, CEO of SalioGen—ASGCT's The Issue

Meet Dr. Mohamed Abou-el-Enein, Editor-in-Chief of Molecular Therapy Methods & Clinical Development | The Molecular Therapy Podcast

Increasing Equitable Access with Hayley Lam, PhD

An Explosive Year for Gene Therapy with ASGCT President Paula Cannon

Reporting on Regulatory Considerations with Journalist Jef Akst

CNS Gene Therapies with Todd Carter, PhD

New Frontiers in Hemophilia Treatments with Lindsey George, MD

Cystic Fibrosis Gene Therapies with CDA Winner Ashley Cooney, PhD

Patient Advocacy with Leah Myers + Jenny Burke

Stem Cell Therapy with Charles Murry, MD, PhD

Communicating the Science with Benjamin McLeod

New Technologies for Gene Targeting + Gene Correction with David Segal, PhD

Welcome to the Annual Meeting with ASGCT President Jeff Chamberlain, PhD

Annual Meeting Soundbites: Coming Soon!

ASGCT 2024 Abstract Highlights with Chris Leidli, Emily Walsh Martin, and Lynnea Olivarez

CMC Strategy with Susan D'Costa, PhD—The Issue

CAR T for Acute Myeloid Leukemia with Dr. Marco Davila—Molecular Therapy Podcast

Regulatory Landscapes in CGT with Sabrina Mogle—ASGCT's The Issue

Hot Topics in CGT with WIRED's Emily Mullin: Annual Meeting Preview

Improving AAV Production with Adam Schieferecke, PhD, and David Schaffer, PhD - Molecular Therapy Podcast

AI in CGT: Previewing the Annual Meeting with Dr. Rory Bricker-Anthony, Chris Leidli, and Catherine Gillespie

The Issue: AAV Immunogenicity with Federico Mingozzi, PhD

Molecular Therapy Podcast: COVID-19 Diagnostics with Dr. Maxim Berezovski

The Issue: Gene Editing Complexities with Tom McCauley, PhD

Molecular Therapy Podcast: Trap and Ambush with Dr. Richard Vile

The Issue: The Patient Experience with Michael Storey, PharmD

Molecular Therapy Podcast: mRNA Vaccines with Dr. Norbert Pardi

Special Episode: Fifth Annual Policy Summit Highlights

Special Episode: What to Expect at ASGCT's Policy Summit with Chris Leidli and Francesca Cook

07 - Luigi Naldini, MD, PhD - Giants of Gene Therapy

06 - Terry Flotte, MD - Giants of Gene Therapy

05 - Jennifer Doudna, PhD - Giants of Gene Therapy

04 - Drew Weissman, MD, PhD - Giants of Gene Therapy

03 - Carl June, MD - Giants of Gene Therapy

02 - Kathy High, MD - Giants of Gene Therapy

01 - David Baltimore, PhD - Giants of Gene Therapy

Giants of Gene Therapy: Episode 0